CatalystAlert

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Search for companies, drugs, and catalysts

Search CatalystAlert

Search for companies, drugs, and catalysts

All Therapeutic Areas
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Rare & Genetic Diseases

56 drugs in pipeline from 10 companies

56

Drugs in Pipeline

10

Companies

7

Upcoming Catalysts

56

Phase 3 Trials

Upcoming Catalysts
Tomorrow
MRKPhase 3

Pembrolizumab Phase 3 Results Expected

pembrolizumab46
Mar 5
CT.gov
00%
2w
PFEPhase 3

docetaxel Phase 3 Results Expected

Docetaxel703
Mar 12
CT.gov
00%
2w
PFEPhase 3

sigvotatug vedotin Phase 3 Results Expected

Sigvotatug Vedotin703
Mar 12
CT.gov
00%
2w
BMYPhase 3
Positive

Repotrectinib Phase 3 Results Expected

Repotrectinib190
Mar 13
CT.gov
2w
MRUSPhase 2

MCLA-129 Phase 2 Results Expected

MCLA-129194
Mar 15
CT.gov
00%
2w
ADVBPhase 3

[18F]PSMA-1007 Phase 3 Results Expected

[18F]PSMA-1007380
Mar 15
CT.gov
00%
3w
RHHBYPhase 2

Tiragolumab Phase 2 Results Expected

Tiragolumab204
Mar 20
CT.gov
00%
Pipeline by Phase
Phase 3
56
Related Conditions
rare diseaseorphangeneticgene therapyhereditarymuscular dystrophycystic fibrosissickle cellhemophiliathalassemiagaucherfabrypompehunter syndromephenylketonuriapkusmaspinal muscular atrophy