Phase 3
Development Phase
1
Upcoming Catalysts
0
Historical Events
1
Regulatory Approvals
Eplontersen Phase 3 Results Expected
Eplontersen • Transthyretin-Mediated Amyloid Cardiomyopathy (ATTR CM)
Target Indication
Transthyretin-Mediated Amyloid Cardiomyopathy (ATTR CM)
Clinical Trial
NCT04136171Last updated: 12/4/2025
Wainzua
Treatment of hereditary transthyretin-mediated amyloidosis (ATTRv) in adult patients with stage 1 or stage 2 polyneuropathy.
View on EMA