
Search for companies, drugs, and catalysts
Search for companies, drugs, and catalysts
Pharmaceutical Preparations · market cap $655M
Research and calibrated estimates, not financial advice — verify before acting.
| Asset | Phase | Indication |
|---|---|---|
| Ataluren | Phase 3 | Duchenne Muscular Dystrophy |
| EPI-743 | Phase 2 | Leigh Syndrome |
| PTC923 | Phase 3 | BH4 Deficiency |
| EPI-589 | Phase 2 | Amyotrophic Lateral Sclerosis |
| EPI-743 400 mg | Phase 2 | Friedreich's Ataxia |
| EPI-743 15 mg/kg | Phase 2 | Leigh Syndrome |
| CNSA-001 | Phase 2 | Gastroparesis |
| Ataluren (PTC124®) | Phase 3 | Cystic Fibrosis |
| Vatiquinone | Phase 3 | Friedreich Ataxia |
| Sepiapterin | Phase 3 | Phenylketonuria |
| PTC124 | Phase 2 | Cystic Fibrosis |
Daily closes through 2026-07-02. Realized vol annualized; max drawdown over ~2 years.
The full dossier is a Pro feature
Thesis, bull & bear, the if-approved scenario, financials, smart-money signals and risks — compiled by CeliA. The catalyst path & pipeline above are free.
See ProApproval odds use historical phase base rates; the if-approved scenario is illustrative (see its note). Figures trace to the sources above — verify before acting.
Data from CatalystAlert (ClinicalTrials.gov, SEC EDGAR, openFDA, Financial Modeling Prep). Compiled by CeliA. Not financial advice.