PTC Therapeutics, Inc.
PTCTNext catalyst
No upcoming catalyst in our data
No upcoming FDA decision, filing or trial readout is on file for PTCT. That does not mean none is planned.
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1 upcoming event in our data (conference).See the timeline
1 upcoming, 2 past
Conference Presentation
PTC Therapeutics announced its executives will present at the Jefferies Global Healthcare Conference on Nov. 16 and the Citi 2026 Global Healthcare Conference in December.
SourceHow PTCT's past catalysts played out
Market Overview
Stock performance and key metrics
PTC Therapeutics, Inc. is a US pharmaceutical company focused on the development of orally administered small molecule drugs and gene therapy which regulate gene expression by targeting post-transcriptional control (PTC) mechanisms in orphan diseases.
WebsiteAtaluren (PTC124®)
Cystic Fibrosis
Vatiquinone
Friedreich Ataxia
Sepiapterin
Phenylketonuria
Ataluren
Duchenne Muscular Dystrophy
PTC923
BH4 Deficiency
PTC124
Cystic Fibrosis
EPI-743
Leigh Syndrome
EPI-589
Amyotrophic Lateral Sclerosis
CNSA-001
Gastroparesis
| Drug Name | Phase | Indication | Designations | Patent |
|---|---|---|---|---|
Ataluren (PTC124®) | Phase 3 | Cystic Fibrosis | - | - |
Vatiquinone | Phase 3 | Friedreich Ataxia | - | - |
Sepiapterin | Phase 3 | Phenylketonuria | - | - |
Ataluren | Phase 3 | Duchenne Muscular Dystrophy | - | - |
PTC923 | Phase 3 | BH4 Deficiency | - | - |
PTC124 | Phase 2 | Cystic Fibrosis | - | - |
EPI-743 | Phase 2 | Leigh Syndrome | - | - |
EPI-589 | Phase 2 | Amyotrophic Lateral Sclerosis | - | - |
CNSA-001 | Phase 2 | Gastroparesis | - | - |
Frequently asked questions
What is in PTC Therapeutics, Inc.'s drug pipeline?→
CatalystAlert tracks 9 drug candidates in PTC Therapeutics, Inc.'s (PTCT) pipeline across Phase 3, Phase 2. Its lead program is Ataluren (Phase 3). Each drug's phase, indication and upcoming catalysts are listed on this page.
When is PTC Therapeutics, Inc.'s next FDA catalyst?→
CatalystAlert tracks every upcoming catalyst for PTC Therapeutics, Inc. (PTCT) — PDUFA decision dates, Phase 1/2/3 trial readouts, FDA advisory committee meetings and NDA/BLA filings — each confidence-rated as confirmed, estimated or AI-detected.
How do I track PTCT biotech catalysts?→
Add PTCT to your CatalystAlert watchlist for alerts ahead of each catalyst, and follow PTC Therapeutics, Inc.'s live catalyst calendar, drug pipeline and clinical-trial timeline on this page — sourced from ClinicalTrials.gov, FDA and SEC filings.