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Phase 3

Development Phase

1

Upcoming Catalysts

0

Historical Events

0

Regulatory Approvals

Upcoming Catalysts
What are catalysts?
Q1 '27
REGNPhase 3

Cemdisiran Phase 3 Est. Readout

Cemdisiran
Q1 2027~QSTALE
CT.gov
00%
Competitive Landscape

3 competitors in Paroxysmal Nocturnal Hemoglobinuria

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Drug Information

Target Indication

Paroxysmal Nocturnal Hemoglobinuria

Clinical Trial

NCT04811716

Last updated: 1/2/2026

Patent & Exclusivity

No patent data available. Pre-approval drugs may not have Orange Book listings.

Drug Science
Mechanism of action & safety profile
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