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PR Newswire Pharma
High ImpactOriginal article

BioMarin Announces Positive Results of Phase 3 VOXZOGO® (vosoritide) Study in Hypochondroplasia Published in NEJM Evidence

Phase 3positiveVOXZOGOPositive
AI Analysis

Summary

BioMarin announced positive Phase 3 CANOPY-HCH-3 results for VOXZOGO (vosoritide) in hypochondroplasia, demonstrating statistically significant improvements across multiple endpoints. Data were published in NEJM Evidence and presented at ESPE 2026.

Clinical Trial Data

Phase

3

Primary Endpoint

Met

Outcome Details

Statistically significant improvements across multiple endpoints in CANOPY-HCH-3 study

Importance:8/10
Sentiment:
0.85
Phase 3 dataPositive resultsHypochondroplasiaNEJM publicationPediatric indicationESPE 2026
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Published by PR Newswire Pharma on September 9, 2026 1:05 PM

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