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PharmaTimes
Original article

NHS backs new treatment option for cystinosis

Regulatoryapproveddelayed-release mercaptaminePositive
AI Analysis

Summary

The NHS has approved delayed-release mercaptamine for routine use as a treatment option for cystinosis. This regulatory approval expands treatment availability for patients with this rare genetic disorder.

Outcome Details

NHS approved delayed-release mercaptamine for routine use in cystinosis

Importance:6/10
Sentiment:
0.70
regulatory approvalNHScystinosismercaptaminerare disease
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Published by PharmaTimes on August 12, 2026 9:30 AM

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