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PR Newswire Clinical Trials
High ImpactOriginal article

BioMarin Announces Positive Results of Phase 3 VOXZOGO® (vosoritide) Study in Hypochondroplasia Published in NEJM Evidence

Phase 3positiveVOXZOGOPositive
AI Analysis

Summary

BioMarin announced positive Phase 3 CANOPY-HCH-3 results for VOXZOGO (vosoritide) in hypochondroplasia, with statistically significant improvements across multiple endpoints. Data were published in NEJM Evidence and presented at ESPE 2026 Annual Meeting.

Clinical Trial Data

Phase

Phase 3

Primary Endpoint

Met

Outcome Details

statistically significant improvements across multiple endpoints

Importance:8/10
Sentiment:
0.85
Phase 3 dataVOXZOGOhypochondroplasiaNEJM Evidence publicationESPE 2026 presentationpositive results
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Published by PR Newswire Clinical Trials on September 9, 2026 1:05 PM

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