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GlobeNewswire Clinical Studies
High ImpactOriginal article

The Lancet Publishes HOPE-3 Data for Capricor Therapeutics’ Deramiocel in Duchenne Muscular Dystrophy

Phase 3positiveDeramiocelPositive
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Summary

Capricor Therapeutics' deramiocel met the primary endpoint in the Phase 3 HOPE-3 trial for Duchenne Muscular Dystrophy, slowing upper limb function decline by 54% versus placebo with clinically meaningful cardiac benefit. The results were published in The Lancet with independent peer review validation.

Clinical Trial Data

Phase

Phase 3

Primary Endpoint

Met

Patients

106

Outcome Details

HOPE-3 Phase 3 trial met primary endpoint, slowing upper limb function decline by 54% versus placebo (PUL 2.0, p=0.03) with clinically meaningful cardiac benefit

Importance:8/10
Sentiment:
0.85
Phase 3 dataDMDprimary endpoint metLancet publicationpeer-reviewed
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Published by GlobeNewswire Clinical Studies on July 29, 2026 2:05 PM

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