All IndicationsApprovedPhase 3Phase 2Phase 2
Achondroplasia
2
Companies
6
Drug Programs
1
Phase 3
0
Upcoming PDUFAs
Competitors
BMRN
BioMarin Pharmaceutical Inc.
Voxzogo
BreakthroughFast TrackOrphan Drug
ASND
Ascendis Pharma A/S
TransCon CNP
ASND
Ascendis Pharma A/S
Navepegritide
ASND
Ascendis Pharma A/S
Placebo for Navepegritide
ASND
Ascendis Pharma A/S
YUVIWEL®
ASND
Ascendis Pharma A/S
YUVIWEL
| Company | Drug | Phase | Designations | Timeline | Trial ID |
|---|---|---|---|---|---|
| BMRN BioMarin Pharmaceutical Inc. | Voxzogo | Approved | BTFTOD | — | — |
| ASND Ascendis Pharma A/S | TransCon CNP | Phase 3 | — | — | — |
| ASND Ascendis Pharma A/S | Navepegritide | Phase 2 | — | — | — |
| ASND Ascendis Pharma A/S | Placebo for Navepegritide | Phase 2 | — | — | — |
| ASND Ascendis Pharma A/S | YUVIWEL® | — | — | — | — |
| ASND Ascendis Pharma A/S | YUVIWEL | — | — | — | — |
Development Stage Distribution
Unknown
2
Approved
1
Phase 3
1
Phase 2
2
PDUFA Timeline
No upcoming PDUFA dates for this indication.
Not financial advice
Signals are probabilistic and based on historical data — past performance doesn't guarantee future results. Do your own research.
