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Approved
Development Phase
0
Upcoming Catalysts
0
Historical Events
1
Regulatory Approvals
No catalyst events have been recorded for this drug yet.
1 competitor in hATTR Amyloidosis
View Full LandscapeTarget Indication
hATTR Amyloidosis
Mechanism of Action
RNAi Therapeutic
Clinical Trial
NCT03759379Last updated: 12/3/2025
Latest Patent Expiry
Patents Listed
13
Exclusivity
Application
NDA 215515Amvuttra
Treatment of hereditary transthyretin-mediated amyloidosis (hATTR amyloidosis) in adult patients with stage 1 or stage 2 polyneuropathy.