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Phase 1/2
Development Phase
0
Upcoming Catalysts
0
Historical Events
0
Regulatory Approvals
No catalyst events have been recorded for this drug yet.
1 competitor in Phenylketonuria
View Full LandscapeTarget Indication
Phenylketonuria
Mechanism of Action
Gene Therapy
Clinical Trial
NCT05235620Last updated: 12/3/2025
No patent data available. Pre-approval drugs may not have Orange Book listings.
Phenylketonurias
Mucopolysaccharidosis IV A
Pain, Post-operative
Anemia Associated With End Stage Renal Disease
Hemophilia A With Inhibitor