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Phase 1/2
Development Phase
0
Upcoming Catalysts
0
Historical Events
0
Regulatory Approvals
No Catalysts Found
No catalyst events have been recorded for this drug yet.
Competitive Landscape
1 competitor in Phenylketonuria
View Full LandscapeDrug Information
Target Indication
Phenylketonuria
Mechanism of Action
Gene Therapy
Clinical Trial
NCT05235620Last updated: 12/3/2025
Patent & Exclusivity
No patent data available. Pre-approval drugs may not have Orange Book listings.
Drug Science
Mechanism of action & safety profile
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