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Phase 2
Development Phase
1
Upcoming Catalysts
Historical Events
0
Regulatory Approvals
Pegtibatinase Phase 2 Results Expected
Pegtibatinase • Homocystinuria
Pegtibatinase Phase 3 Results Expected
Target Indication
Homocystinuria
Clinical Trial
Last updated: 12/4/2025
TVTX
Travere Therapeutics, Inc.
Focal Segmental Glomerulosclerosis
Immunoglobulin A Nephropathy