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Drugs in Pipeline
6
Phase 3 Programs
2
Upcoming Catalysts
Next Catalyst
Mar 15, 2026
AOC 1001 (del-desiran)
DM1
AOC-1020
Facioscapulohumeral Muscular Dystrophy
AOC 1044
Duchenne Muscular Dystrophy
AOC 1001
AOC 1020
FSHD
Placebo
2 upcoming, 0 past
Primary completion for AOC 1001 (del-desiran) trial (NCT06411288) in DM1
Primary completion for AOC 1020 trial (NCT05747924) in FSHD