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PR Newswire Biotech
Original article

Hochpräzise Basen-Editierungstherapie zeigt dauerhafte VOC-freie Wirksamkeit und günstige Sicherheit bei Sichelzellanämie

Data ReadoutpositiveCS-206Positive
AI Analysis

Summary

CorrectSequence Therapeutics reported positive 15-month follow-up data for CS-206, showing sustained vaso-occlusive crisis-free efficacy and favorable safety profile in sickle cell anemia patients.

Clinical Trial Data

Primary Endpoint

Met

Outcome Details

15-month follow-up data showing sustained VOC-free efficacy and favorable safety

Importance:7/10
Sentiment:
0.80
base editingsickle cell diseaseclinical datagene therapyvaso-occlusive crisis

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Published by PR Newswire Biotech on June 3, 2026 1:16 PM

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